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RecruitingInterventionalPhase 3

High-dose Vitamin D Supplementation for ADT-Induced Bone Loss in Older Prostate Cancer Patients

NCT ID: NCT05838716Sponsor: University of RochesterLast updated: 2026-01-15

Summary

This phase III trial tests whether high-dose vitamin D works in treating androgen-deprivation therapy (ADT)-induced bone loss in patients with prostate cancer who are undergoing androgen-deprivation therapy. Vitamins are substances that the body needs to grow and develop normally. Vitamin D helps the body absorb calcium. Calcium is one of the main building blocks of bone. A lack of vitamin D can lead to bone diseases such as osteoporosis or rickets. This trial may help researchers determine if high-dose vitamin D helps keep bones strong, lowers number of falls, and lessens fatigue in men getting androgen-deprivation therapy.

Detailed description

PRIMARY OBJECTIVES: I. To evaluate the effect of high-dose vitamin D (HDVD) supplementation in prostate cancer patients on ADT-induced bone mineral density loss in the total hip over 52 weeks as measured by dual-energy x-ray absorptiometry (DXA). II. To evaluate the effect of HDVD supplementation in prostate cancer patients on ADT-induced bone mineral density loss in the femoral neck, distal radius, and lumbar spine (L1-L4) over 52 weeks as measured by DXA. SECONDARY OBJECTIVES: I. To evaluate the effect of HDVD supplementation on falls over 52 weeks as measured by the Falls History questionnaire. II. To evaluate the effect of HDVD supplementation on fractures over 52 weeks as determined by the Clinical Record Information - Follow-up Form. III. To evaluate the effect of HDVD supplementation on quality of life over 52 weeks as measured by the Functional Assessment of Cancer Therapy- Prostate (FACT-P). EXPLORATORY OBJECTIVE: I. To evaluate the effect of HDVD supplementation on pain, fatigue, sleep, and activities of daily living over 52 weeks as measured by patient-reported outcomes. OUTLINE: After undergoing collection of blood and DXA scan, patients are randomized to 1 of 2 arms. ARM I: Patients receive HDVD orally (PO) once a week (QW) for 52 weeks. Patients also undergo collection of blood and DXA scan on study. ARM II: Patients receive placebo PO QW for 52 weeks. Patients also undergo collection of blood and DXA scan on study.

Arms & interventions

  • ProcedureBiospecimen Collection

    Undergo collection of blood

  • Dietary SupplementD Vitamin

    Given PO

  • ProcedureDual X-ray Absorptiometry

    Undergo DXA scan

  • DrugPlacebo Administration

    Given PO

  • OtherQuality-of-Life Assessment

    Ancillary studies

  • OtherQuestionnaire Administration

    Ancillary studies

Outcome measures

Primary

  • Reduction of bone mineral density (BMD) loss as measured at the total hip

    Will determine the efficacy of high-dose vitamin D (HDVD) supplementation versus placebo in reducing BMD loss as measured at the total hip via dual-energy x-ray absorptiometry (DXA) at 52 weeks. Will use analysis of covariance (ANCOVA) with group (vitamin D or placebo) as the main factor, baseline timepoint (\[T\]1) BMD as covariate, and week 52 (T3) BMD as the outcome. Study site will be included as a random effect independent of residual error. An initial linear mixed model (LMM) will be fit using Restricted Maximum Likelihood (REML) estimation. The significance of the variance due to study site will be tested using the Wald Test.

    Time frame: At 52 weeks

  • Reduction of BMD loss as measured at the femoral neck

    Will determine the efficacy of HDVD supplementation versus placebo in reducing BMD loss as measured at the femoral neck via DXA at 52 weeks. Will use ANCOVA with group (vitamin D or placebo) as the main factor, baseline (T1) BMD as covariate, and week 52 (T3) BMD as the outcome. Study site will be included as a random effect independent of residual error. An initial LMM will be fit using REML estimation. The significance of the variance due to study site will be tested using the Wald Test.

    Time frame: At 52 weeks

  • Reduction of BMD loss as measured at the distal radius

    Will determine the efficacy of HDVD supplementation versus placebo in reducing BMD loss as measured at the distal radius via DXA at 52 weeks. Will use ANCOVA with group (vitamin D or placebo) as the main factor, baseline (T1) BMD as covariate, and week 52 (T3) BMD as the outcome. Study site will be included as a random effect independent of residual error. An initial LMM will be fit using REML estimation. The significance of the variance due to study site will be tested using the Wald Test.

    Time frame: At 52 weeks

  • Reduction of BMD loss as measured at the lumbar spine

    Will determine the efficacy of HDVD supplementation versus placebo in reducing BMD loss as measured at the lumbar spine via DXA at 52 weeks. Will use ANCOVA with group (vitamin D or placebo) as the main factor, baseline (T1) BMD as covariate, and week 52 (T3) BMD as the outcome. Study site will be included as a random effect independent of residual error. An initial LMM will be fit using REML estimation. The significance of the variance due to study site will be tested using the Wald Test.

    Time frame: At 52 weeks

Secondary

  • Change in falls

    Time frame: Baseline up to 52 weeks

  • Change in fractures

    Time frame: Baseline up to 52 weeks

  • Change in quality of life

    Time frame: Baseline up to 52 weeks

Eligibility criteria

Sex: MaleAge: 50 Years and olderHealthy volunteers: No
Inclusion Criteria: * Be diagnosed with Stage I-IV prostate cancer without metastases to bone (lymph node involvement and prior diagnosis of a primary cancer is allowed) * Be age 50 years or older * Be starting ADT or have received their first ADT treatment in the past 6 months, with a total of at least 6 planned months of treatment (both luteinizing hormone-releasing hormone \[LHRH\] antagonists and LHRH agonists are permitted) * Have a total serum vitamin D between 10 and 32 ng/ml * Have a total serum calcium of less than or equal to 10.5 mg/dl * Have a normal GFR (glomerular filtration rate \> 30ml) * Agree not to take calcium and/or vitamin D supplements for the duration of the intervention other than those provided by the study * Be able to provide written informed consent * Be able to swallow pills and capsules * Be able to speak and read English Exclusion Criteria: * Have long term (greater than 3 months) use of any pharmacologic bone-modifying agent including but not limited to oral or intravenous (IV) bisphosphonates, denosumab, or teriparatide prior to enrollment * Have a diagnosis of stage IV chronic kidney disease * Have a diagnosis of grade II or greater hypercalcemia (serum calcium greater than 11.5 mg/dl) * Have a history of hypercalcemia or vitamin D toxicity/sensitivity

Study locations (51)

Helen F Graham Cancer Center

Newark, Delaware, 19713

Recruiting
Site Public Contact · Contact
Gregory A. Masters · Principal Investigator

Medical Oncology Hematology Consultants PA

Newark, Delaware, 19713

Recruiting
Site Public Contact · Contact
Gregory A. Masters · Principal Investigator

Carle at The Riverfront

Danville, Illinois, 61832

Recruiting
Site Public Contact · Contact
Vamsi K. Vasireddy · Principal Investigator

Cancer Care Specialists of Illinois - Decatur

Decatur, Illinois, 62526

Recruiting
Site Public Contact · Contact
Bryan A. Faller · Principal Investigator

Carle Physician Group-Effingham

Effingham, Illinois, 62401

Recruiting
Site Public Contact · Contact
Vamsi K. Vasireddy · Principal Investigator

Carle Physician Group-Mattoon/Charleston

Mattoon, Illinois, 61938

Recruiting
Site Public Contact · Contact
Vamsi K. Vasireddy · Principal Investigator

Cancer Care Center of O'Fallon

O'Fallon, Illinois, 62269

Recruiting
Site Public Contact · Contact
Bryan A. Faller · Principal Investigator

Carle Cancer Center

Urbana, Illinois, 61801

Recruiting
Site Public Contact · Contact
Vamsi K. Vasireddy · Principal Investigator

University of Kansas Cancer Center

Kansas City, Kansas, 66160

Recruiting
Site Public Contact · Contact
Elizabeth M. Wulff · Principal Investigator

University of Kansas Cancer Center-Overland Park

Overland Park, Kansas, 66210

Recruiting
Site Public Contact · Contact
Elizabeth M. Wulff · Principal Investigator

University of Kansas Health System Saint Francis Campus

Topeka, Kansas, 66606

Recruiting
Site Public Contact · Contact
Elizabeth M. Wulff · Principal Investigator

University of Kansas Hospital-Westwood Cancer Center

Westwood, Kansas, 66205

Recruiting
Site Public Contact · Contact
Elizabeth M. Wulff · Principal Investigator

Louisiana State University Health Science Center

New Orleans, Louisiana, 70112

Recruiting
Site Public Contact · Contact
Rajasree P. Chowdry · Principal Investigator

University Medical Center New Orleans

New Orleans, Louisiana, 70112

Recruiting
Site Public Contact · Contact
Rajasree P. Chowdry · Principal Investigator

Ochsner Medical Center Jefferson

New Orleans, Louisiana, 70121

Recruiting
Site Public Contact · Contact
Brian T. Halbert · Principal Investigator

Mercy Hospital

Coon Rapids, Minnesota, 55433

Recruiting
Site Public Contact · Contact
Sarah E. Jax · Principal Investigator

Minnesota Oncology Hematology PA-Maplewood

Maplewood, Minnesota, 55109

Recruiting
Site Public Contact · Contact
Sarah E. Jax · Principal Investigator

Saint John's Hospital - Healtheast

Maplewood, Minnesota, 55109

Recruiting
Site Public Contact · Contact
Sarah E. Jax · Principal Investigator

Park Nicollet Clinic - Saint Louis Park

Saint Louis Park, Minnesota, 55416

Recruiting
Site Public Contact · Contact
Sarah E. Jax · Principal Investigator

Regions Hospital

Saint Paul, Minnesota, 55101

Recruiting
Site Public Contact · Contact
Sarah E. Jax · Principal Investigator

Ridgeview Medical Center

Waconia, Minnesota, 55387

Recruiting
Site Public Contact · Contact
Sarah E. Jax · Principal Investigator

University of Kansas Cancer Center - North

Kansas City, Missouri, 64154

Recruiting
Site Public Contact · Contact
Elizabeth M. Wulff · Principal Investigator

University of Kansas Cancer Center - Lee's Summit

Lee's Summit, Missouri, 64064

Recruiting
Site Public Contact · Contact
Elizabeth M. Wulff · Principal Investigator

Mercy Hospital Saint Louis

St Louis, Missouri, 63141

Recruiting
Site Public Contact · Contact
Jay W. Carlson · Principal Investigator

OptumCare Cancer Care at Charleston

Las Vegas, Nevada, 89102

Recruiting
Site Public Contact · Contact
Khawaja S. Jahangir · Principal Investigator

CarolinaEast Medical Center

New Bern, North Carolina, 28561

Recruiting
Site Public Contact · Contact
Seth M. Miller · Principal Investigator

Nash UNC HealthCare

Rocky Mount, North Carolina, 27804

Recruiting
Site Public Contact · Contact
Elie B. Choufani · Principal Investigator

Adena Regional Medical Center

Chillicothe, Ohio, 45601

Recruiting
Site Public Contact · Contact
Aruna C. Gowda · Principal Investigator

Geisinger Cancer Center Dickson City

Dickson City, Pennsylvania, 18519

Recruiting
Site Public Contact · Contact
Heath B. Mackley · Principal Investigator

Community Medical Center

Scranton, Pennsylvania, 18510

Recruiting
Site Public Contact · Contact
Heath B. Mackley · Principal Investigator

Geisinger Wyoming Valley/Henry Cancer Center

Wilkes-Barre, Pennsylvania, 18711

Recruiting
Site Public Contact · Contact
Heath B. Mackley · Principal Investigator

Gibbs Cancer Center-Gaffney

Gaffney, South Carolina, 29341

Recruiting
Site Public Contact · Contact
Michael Humeniuk · Principal Investigator

Saint Francis Hospital

Greenville, South Carolina, 29601

Recruiting
Site Public Contact · Contact
Stephen H. Dyar · Principal Investigator

Saint Francis Cancer Center

Greenville, South Carolina, 29607

Recruiting
Site Public Contact · Contact
Stephen H. Dyar · Principal Investigator

Gibbs Cancer Center-Pelham

Greer, South Carolina, 29651

Recruiting
Site Public Contact · Contact
Michael Humeniuk · Principal Investigator

Spartanburg Medical Center

Spartanburg, South Carolina, 29303

Recruiting
Site Public Contact · Contact
Michael Humeniuk · Principal Investigator

SMC Center for Hematology Oncology Union

Union, South Carolina, 29379

Recruiting
Site Public Contact · Contact
Michael Humeniuk · Principal Investigator

Regional Cancer Center at Johnson City Medical Center

Johnson City, Tennessee, 37604

Recruiting
Site Public Contact · Contact
Asheesh Shipstone · Principal Investigator

Ballad Health Cancer Care - Kingsport

Kingsport, Tennessee, 37660

Recruiting
Site Public Contact · Contact
Asheesh Shipstone · Principal Investigator

Ballad Health Cancer Care - Bristol

Bristol, Virginia, 24201

Recruiting
Site Public Contact · Contact
Asheesh Shipstone · Principal Investigator

Bon Secours Memorial Regional Medical Center

Mechanicsville, Virginia, 23116

Recruiting
Site Public Contact · Contact
William J. Irvin · Principal Investigator

Bon Secours Saint Francis Medical Center

Midlothian, Virginia, 23114

Recruiting
Site Public Contact · Contact
William J. Irvin · Principal Investigator

Bon Secours Saint Mary's Hospital

Richmond, Virginia, 23226

Recruiting
Site Public Contact · Contact
William J. Irvin · Principal Investigator

Bon Secours Cancer Institute at Reynolds Crossing

Richmond, Virginia, 23230

Recruiting
Site Public Contact · Contact
William J. Irvin · Principal Investigator

VCU Massey Cancer Center at Stony Point

Richmond, Virginia, 23235

Recruiting
Site Public Contact · Contact
Asit K. Paul · Principal Investigator

VCU Massey Comprehensive Cancer Center

Richmond, Virginia, 23298

Recruiting
Site Public Contact · Contact
Asit K. Paul · Principal Investigator

Carilion Roanoke Memorial Hospital

Roanoke, Virginia, 24033

Recruiting
Site Public Contact · Contact
Asit K. Paul · Principal Investigator

Saint Vincent Hospital Cancer Center Green Bay

Green Bay, Wisconsin, 54301

Recruiting
Site Public Contact · Contact
Brian L. Burnette · Principal Investigator

Saint Vincent Hospital Cancer Center at Saint Mary's

Green Bay, Wisconsin, 54303

Recruiting
Site Public Contact · Contact
Brian L. Burnette · Principal Investigator

Gundersen Lutheran Medical Center

La Crosse, Wisconsin, 54601

Recruiting
Site Public Contact · Contact
Kurt Oettel · Principal Investigator

Saint Vincent Hospital Cancer Center at Sturgeon Bay

Sturgeon Bay, Wisconsin, 54235-1495

Recruiting
Site Public Contact · Contact
Brian L. Burnette · Principal Investigator