A Phase Ib/II Study of AZD0120, Dual-Targeting Autologous Chimeric Antigen Receptor T-cell (CAR T) Therapy Directed Against CD19 and B-cell Maturation Antigen (BCMA) in Participants With Relapsed/Refractory Multiple Myeloma (DURGA-1)
Summary
This trial is a Phase 1b/2, open-label, multicenter study of AZD0120, a CD19/BCMA dual CAR T-cell therapy, in adult subjects with relapsed/refractory multiple myeloma.
Detailed description
Phase 1b aims to evaluate the safety, tolerability, pharmacokinetic characteristics, pharmacodynamic effect, and immunogenicity in subjects with relapsed/refractory multiple myeloma and determine the recommended Phase 2 dose of AZD0120. Phase II aims to evaluate the efficacy of AZD0120, and to further characterize the safety, pharmacodynamic effects, immunogenicity, and changes in health-related quality of life parameters in subjects with relapsed/refractory multiple myeloma.
Arms & interventions
- BiologicalAZD0120
AZD0120 is a BCMA/CD19 dual CAR T product under investigation for the treatment of participants with RRMM.
Outcome measures
Primary
Phase 1b: Adverse Events (AEs)
The incidence and severity of AEs.
Time frame: Through study completion, a minimum of 2 years.
Phase 1b: Dose-Limiting Toxicities (DLTs)
The DLT evaluation period is defined as the first 28 days after infusion.
Time frame: 28 days
Phase 2: Objective Response Rate (ORR)
Defined as the proportion of participants who achieved partial response (PR) or better by the International Myeloma Working Group (IMWG) response criteria.
Time frame: Through study completion, a minimum of 2 years.
Secondary
Phase 1b and 2: Complete response rate (CRR)
Time frame: Through study completion, a minimum of 2 years.
Phase 1b and 2: Time to response (TTR)
Time frame: Through study completion, a minimum of 2 years.
Phase 1b: Objective Response Rate (ORR)
Time frame: Through study completion, a minimum of 2 years.
Phase 1b and 2: Minimal Residual Disease (MRD) negative Complete Response (CR) rate
Time frame: Through study completion, a minimum of 2 years.
Phase 1b and 2: Minimal Residual Disease (MRD) negative Complete Response (CR) rate at 12 months
Time frame: 12 months
Phase 1b and 2: Duration of response (DOR)
Time frame: Through study completion, a minimum of 2 years.
Phase 1b and 2: Progression-free survival (PFS)
Time frame: Through study completion, a minimum of 2 years.
Phase 1b and 2: Overall survival (OS)
Time frame: Through study completion, a minimum of 2 years.
Phase 2: Adverse Events (AEs)
Time frame: Through study completion, a minimum of 2 years.
Ph1b and 2: Pharmacokinetics - AUC
Time frame: Through study completion, a minimum of 2 years.
Ph1b and 2: Pharmacokinetics - Clast
Time frame: Through study completion, a minimum of 2 years.
Ph1b and 2: Pharmacokinetics - Cmax
Time frame: Through study completion, a minimum of 2 years.
Ph1b and 2: Pharmacokinetics - Tlast
Time frame: Through study completion, a minimum of 2 years.
Ph1b and 2: Pharmacokinetics - Tmax
Time frame: Through study completion, a minimum of 2 years
Ph1b and 2: Humoral Immunogenicity
Time frame: Through study completion, a minimum of 2 years.
Phase 2: European Organization for Research and Treatment of Cancer Quality of Life Questionnaire IL355 (EORTC IL355)
Time frame: Through study completion, a minimum of 2 years.
Phase 2: European Organization for Research and Treatment of Cancer Quality of Life Questionnaire EORTC IL356
Time frame: Through study completion, a minimum of 2 years.
Eligibility criteria
Study locations (36)
Research Site
Birmingham, Alabama, 35233
Research Site
Phoenix, Arizona, 85054
Research Site
La Jolla, California, 92037
Research Site
Los Angeles, California, 90095
Research Site
San Francisco, California, 94143
Research Site
Aurora, Colorado, 80045
Research Site
Denver, Colorado, 80218
Research Site
Jacksonville, Florida, 32224
Research Site
Miami, Florida, 33136
Research Site
Tampa, Florida, 33612
Research Site
Atlanta, Georgia, 30322
Research Site
Chicago, Illinois, 60637
Research Site
Iowa City, Iowa, 52242
Research Site
Boston, Massachusetts, 02114
Research Site
Boston, Massachusetts, 02215
Research Site
Ann Arbor, Michigan, 48109
Research Site
Detroit, Michigan, 48202
Research Site
Minneapolis, Minnesota, 55455
Research Site
Rochester, Minnesota, 55905
Research Site
Omaha, Nebraska, 68198
Research Site
Hackensack, New Jersey, 07601
Research Site
Buffalo, New York, 14203
Research Site
New York, New York, 10065
Research Site
Stony Brook, New York, 11794
Research Site
Charlotte, North Carolina, 28204
Research Site
Durham, North Carolina, 27705
Research Site
Nashville, Tennessee, 37203
Research Site
Nashville, Tennessee, 37232
Research Site
Austin, Texas, 78704
Research Site
Dallas, Texas, 75390
Research Site
Houston, Texas, 77030
Research Site
Salt Lake City, Utah, 84112
Research Site
Charlottesville, Virginia, 22908
Research Site
Edmonds, Washington, 98026
Research Site
Seattle, Washington, 98109
Research Site
Milwaukee, Wisconsin, 53226