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RecruitingInterventionalPhase 3

A Phase 3, Randomized, Multicenter, Open-Label Study of IDRX-42 (GSK6042981) Versus Sunitinib in Participants With Metastatic and/or Unresectable Gastrointestinal Stromal Tumors (GIST) After Imatinib Therapy (StrateGIST 3)

NCT ID: NCT07218926Sponsor: GlaxoSmithKlineLast updated: 2026-06-12

Summary

The purpose of this study is to find out if a new drug, called IDRX-42 (also known as GSK6042981), is effective in treating adults with a type of cancer called Gastrointestinal Stromal Tumors (GIST) when compared to another drug named sunitinib. The study will see if IDRX-42 works well and is safe for participants whose GIST has spread or cannot be surgically removed, and who have already taken the drug imatinib. Participants whose disease worsens after receiving sunitinib in this study may cross over to receive GSK6042981, at investigator's discretion and if additional eligibility criteria are met.

Arms & interventions

  • DrugIDRX-42

    IDRX-42 will be administered.

  • DrugSunitinib

    Sunitinib will be administered.

Outcome measures

Primary

  • Progression-Free Survival (PFS)

    PFS is defined as time from the date of randomization to the date of disease progression or death due to any cause, whichever occurs first.

    Time frame: Up to approximately 130 weeks

Secondary

  • Overall Survival (OS)

    Time frame: Up to approximately 261 weeks

  • Progression-Free Survival (PFS)

    Time frame: Up to approximately 261 weeks

  • Confirmed Overall Objective Response Rate (ORR)

    Time frame: Up to approximately 261 weeks

  • Time to Response (TTR)

    Time frame: Up to approximately 261 weeks

  • Time from initial study randomization to second disease progression or death after starting the next line of treatment (PFS2)

    Time frame: Up to approximately 261 weeks

  • Change From Baseline in European Organization for Research and Treatment of Cancer Quality of Life Questionnaire 30-item Core Module (EORTC QLQ-C30)

    Time frame: Baseline (Day 1) and up to approximately 261 weeks

  • Time To Confirmed Deterioration (TTCD)

    Time frame: Up to approximately 261 weeks

  • Plasma concentrations of IDRX-42 (GSK6042981)

    Time frame: Up to approximately 261 weeks

  • Number of Participants with Treatment Emergent Adverse Events (TEAEs) and Serious Adverse Events (SAEs)

    Time frame: Up to approximately 261 weeks

  • Number of Participants with TEAEs and SAEs by severity

    Time frame: Up to approximately 261 weeks

  • Number of Participants with dose reductions, interruptions and discontinuation of study treatment due to toxicity

    Time frame: Up to approximately 261 weeks

  • Number of participants with symptomatic adverse events (AEs), by severity, as measured by the Patient-reported outcome Common Terminology Criteria for Adverse Events (PRO-CTCAE)

    Time frame: Up to approximately 261 weeks

  • Number of participants with bothersome AEs/tolerability as measured by the Functional Assessment of Cancer Therapy - General (FACT-GP5)

    Time frame: Up to approximately 261 weeks

Eligibility criteria

Sex: AllAge: 18 Years and olderHealthy volunteers: No
Inclusion Criteria: * Participants with histologically or cytologically confirmed GIST that is metastatic and/or surgically unresectable. * Documented disease progression on or intolerance to imatinib administered for first-line treatment of unresectable/metastatic disease. * Documented mutation status of KIT and/or PDGFRA using a tissue based next-generation sequencing or polymerase chain reaction (PCR) assay. * Tumor tissue must be available for retrospective biomarker analysis. Sample may be archival or new biopsy. Exclusion Criteria: * GIST that is both KIT and PDGFRA wild-type or known to harbor an activating PDGFRA exon 18 mutation. * Known untreated or active central nervous system metastases. * Participants with a known allergy or hypersensitivity to any component of IDRX-42 (GSK6042981) or sunitinib. Participants with a history of Stevens-Johnson syndrome on a prior Tyrosine kinase inhibitor (TKI) are excluded. * Has a malignancy (except disease under study) that has progressed or required active treatment within the past 24 months except for basal cell or squamous cell carcinomas of the skin or in-situ carcinomas (e.g., breast, cervix, bladder) that have been resected with no evidence of metastatic disease.

Study locations (36)

GSK Investigational Site

Phoenix, Arizona, 85054

Recruiting
US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Mahesh Seetharam · Principal Investigator

GSK Investigational Site

La Jolla, California, 92093

Recruiting
US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Adam Burgoyne · Principal Investigator

GSK Investigational Site

Los Angeles, California, 90048

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
James Hu · Principal Investigator

GSK Investigational Site

San Francisco, California, 94158

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Brian Schulte · Principal Investigator

GSK Investigational Site

New Haven, Connecticut, 06520

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Philippos Costa · Principal Investigator

GSK Investigational Site

Jacksonville, Florida, 41076

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Steven Attia · Principal Investigator

GSK Investigational Site

Miami, Florida, 33136

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Jonathan Trent · Principal Investigator

GSK Investigational Site

Orlando, Florida, 32806

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Jacobo Hincapie-Echeverri · Principal Investigator

GSK Investigational Site

Tampa, Florida, 33612

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Mauricio Ribeiro · Principal Investigator

GSK Investigational Site

Iowa City, Iowa, 52242

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
John Rieth · Principal Investigator

GSK Investigational Site

Overland Park, Kansas, 66210

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Benjamin Powers · Principal Investigator

GSK Investigational Site

Boston, Massachusetts, 02114-2696

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Edwin Choy · Principal Investigator

GSK Investigational Site

Boston, Massachusetts, 02215

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Suzanne George · Principal Investigator

GSK Investigational Site

Ann Arbor, Michigan, 48109

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Scott Schuetze · Principal Investigator

GSK Investigational Site

Rochester, Minnesota, 55905

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Thanh Ho · Principal Investigator

GSK Investigational Site

St Louis, Missouri, 63108

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Mia Weiss · Principal Investigator

GSK Investigational Site

Omaha, Nebraska, 68130

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Kirsten Leu · Principal Investigator

GSK Investigational Site

Lake Success, New York, 11042

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Tony Philip · Principal Investigator

GSK Investigational Site

New York, New York, 10032

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Lanyi Chen · Principal Investigator

GSK Investigational Site

New York, New York, 10065

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Ciara Kelly · Principal Investigator

GSK Investigational Site

Rochester, New York, 14642

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Adrienne Victor · Principal Investigator

GSK Investigational Site

Durham, North Carolina, 27710

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Juneko Grilley-Olson · Principal Investigator

GSK Investigational Site

Columbus, Ohio, 43210

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Gabriel Tinoco · Principal Investigator

GSK Investigational Site

Portland, Oregon, 97239

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Michael Heinrich · Principal Investigator

GSK Investigational Site

Philadelphia, Pennsylvania, 19106

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Daniel Lefler · Principal Investigator

GSK Investigational Site

Philadelphia, Pennsylvania, 19111

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Margaret Von Mehren · Principal Investigator

GSK Investigational Site

Pittsburgh, Pennsylvania, 15232

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Melissa Burgess · Principal Investigator

GSK Investigational Site

Spartanburg, South Carolina, 29307

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Ki Young Chung · Principal Investigator

GSK Investigational Site

Knoxville, Tennessee, 37920

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Saikrishna Gadde · Principal Investigator

GSK Investigational Site

Dallas, Texas, 75246

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Laith Abushahin · Principal Investigator

GSK Investigational Site

Houston, Texas, 77030

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Neeta Somaiah · Principal Investigator

GSK Investigational Site

Santa Monica, Texas, 90404

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Arun Singh · Principal Investigator

GSK Investigational Site

Salt Lake City, Utah, 84106

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Stephan Kendall · Principal Investigator

GSK Investigational Site

Charlottesville, Virginia, 22903

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US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Ludimila Cavalcante · Principal Investigator

GSK Investigational Site

Seattle, Washington, 98109

Recruiting
US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Min Park · Principal Investigator

GSK Investigational Site

Tacoma, Washington, 98405

Recruiting
US GSK Clinical Trials Call Center · Contact
EU GSK Clinical Trials Call Centre · Contact
Katherine Martin · Principal Investigator